neurodegenerative diseases

Zevra snags FDA approval for new lysosomal storage disorder med

The FDA has approved Zevra’s arimoclomol to treat the rare condition Niemann-Pick disease type C in conjunction with J&J's enzyme inhibitor miglustat.

Fraiser Kansteiner Sep 20, 2024 1:54pm

Amylyx to pull failed ALS drug from market, cut 70% of staff

Apr 4, 2024 10:06am

Is treatment for multiple sclerosis about to change fundamentally?

Sep 23, 2024 9:00am